Throughout the last decade, researchers have made great progress studying how the proximity, or physical closeness, of proteins inside a cell influences processes like transcription, signalling and protein folding.
US FDA approval based on NEURO-TTRansform Phase III results showing Wainua demonstrated consistent and sustained benefit improving neuropathy impairment and quality of life. Additional regulatory reviews underway in rest of world.
Translational science is the process of translating research discovery into actionable insights in the clinic, while leveraging clinical data for further discovery to benefit patients.
Clinical research is key to unlocking new medicines with potential to transform outcomes across many diseases. However, this process has potential to generate up to 100 million tons of carbon dioxide equivalent emissions per year – similar to the yearly emissions of a country the size of Belgium.
The kidneys play a critical role in the body, removing toxins and waste, controlling blood pressure, and balancing fluids, salts, and minerals, to ensure optimal conditions for many of the body’s organ systems.
The ever-evolving infectious disease landscape requires researchers to move quickly to adapt and develop solutions to prevent people from experiencing severe outcomes of disease.
Data demonstrated effective control of intravascular and extravascular haemolysis through 48 weeks. Results showed increase in mean haemoglobin levels were maintained through 48 weeks.